
    a pre-planned futility analysis indicated lack of efficacy in study nct03039686 and led to
    discontinuation of both ongoing studies in dmd.
  
['muscular dystrophy (dmd)']
['ro7239361', 'placebo']

        Inclusion Criteria:

          -  Diagnosed with DMD

          -  Able to walk without assistance

          -  Able to walk up 4 stairs in 8 seconds or less

          -  Weigh at least 15 kg

          -  Taking corticosteroids for DMD

        Exclusion Criteria:

          -  Ejection fraction < 55% on echocardiogram, based on central read

          -  Any behavior or mental issue that will affect the ability to complete the required
             study procedures

          -  Previously or currently taking medications like androgens or human growth hormone

          -  Use of a ventilator during the day

          -  Unable to have blood samples collected or receive an injection under the skin

          -  Treatment with exon skipping therapies 6 months prior to study start

          -  Treatment with ataluren or any investigational drug currently or within 5 half-lives
             prior to study start
      